发明授权
- 专利标题: METHODS AND COMPOUNDS USEFUL IN CONDITIONS RELATED TO REPEAT EXPANSION
- 专利标题(中): 方法和化合物与重复扩增相关疾病
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申请号: EP12827475.0申请日: 2012-08-29
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公开(公告)号: EP2751269B1公开(公告)日: 2016-03-23
- 发明人: PRAKASH, Thazha, P. , SWAYZE, Eric, E. , COREY, David , YU, Dongbo
- 申请人: Ionis Pharmaceuticals, Inc. , Board of Regents of the University of Texas System
- 申请人地址: 2855 Gazelle Court Carlsbad, CA 92010 US
- 专利权人: Ionis Pharmaceuticals, Inc.,Board of Regents of the University of Texas System
- 当前专利权人: Ionis Pharmaceuticals, Inc.,Board of Regents of the University of Texas System
- 当前专利权人地址: 2855 Gazelle Court Carlsbad, CA 92010 US
- 代理机构: Carpmaels & Ransford LLP
- 优先权: US201161528719P 20110829
- 国际公布: WO2013033223 20130307
- 主分类号: C12N15/11
- IPC分类号: C12N15/11 ; C07H21/04 ; C12N5/00
摘要:
Described are compounds and methods useful for the treatment and investigation of diseases and disorders associated with expanded repeat-containing RNA molecules.
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