- 专利标题: TREATMENT OF FABRY DISEASE IN ERT-NAIVE AND ERT-EXPERIENCED PATIENTS
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申请号: EP23219947.1申请日: 2017-07-19
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公开(公告)号: EP4356911A1公开(公告)日: 2024-04-24
- 发明人: Castelli, Jeff
- 申请人: Amicus Therapeutics, Inc.
- 申请人地址: US Philadelphia, PA 19104 3675 Market Street
- 专利权人: Amicus Therapeutics, Inc.
- 当前专利权人: Amicus Therapeutics, Inc.
- 当前专利权人地址: US Philadelphia, PA 19104 3675 Market Street
- 代理机构: Hoffmann Eitle
- 优先权: US 201615213920 2016.07.19
- 分案原申请号: 17745612.6 2017.07.19
- 主分类号: A61K31/445
- IPC分类号: A61K31/445 ; A61P9/00 ; A61P3/00 ; A61P13/12
摘要:
Provided are dosing regimens for the treatment of Fabry disease in a patient. Certain methods relate to the treatment of ERT-experienced or ERT-naive Fabry patients. Certain methods comprise administering to the patient about 123 mg free base equivalent of migalastat for improving left ventricular mass and/or improving podocyte globotriaosylceramide.
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