- 专利标题: TREATMENT OF FABRY DISEASE IN ERT-NAIVE AND ERT-EXPERIENCED PATIENTS
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申请号: EP24168026.3申请日: 2017-07-19
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公开(公告)号: EP4389213A2公开(公告)日: 2024-06-26
- 发明人: Castelli, Jeff
- 申请人: Amicus Therapeutics, Inc.
- 申请人地址: US Philadelphia, PA 19104 3675 Market Street
- 专利权人: Amicus Therapeutics, Inc.
- 当前专利权人: Amicus Therapeutics, Inc.
- 当前专利权人地址: US Philadelphia, PA 19104 3675 Market Street
- 代理机构: Hoffmann Eitle
- 优先权: US 1615213920 2016.07.19
- 分案原申请号: 17745612.6 2017.07.19
- 主分类号: A61P13/12
- IPC分类号: A61P13/12
摘要:
Provided are dosing regimens for the treatment of Fabry disease in a patient. Certain methods relate to the treatment of ERT-experienced or ERT-naïve Fabry patients. Certain methods comprise administering to the patient about 123 mg free base equivalent of migalastat for improving left ventricular mass and/or improving podocyte globotriaosylceramide.
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