- 专利标题： RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
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申请号： US18509440申请日： 2023-11-15
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公开(公告)号： US20240279652A1公开(公告)日： 2024-08-22
- 发明人: Kallanthottathil G. Rajeev , Tracy Zimmermann , Muthiah Manoharan , Martin A. Maier , Satyanarayana Kuchimanchi , Klaus Charisse
- 申请人： Alnylam Pharmaceuticals, Inc.
- 申请人地址： US MA Cambridge
- 专利权人： Alnylam Pharmaceuticals, Inc.
- 当前专利权人： Alnylam Pharmaceuticals, Inc.
- 当前专利权人地址： US MA Cambridge
- 主分类号： C12N15/113
- IPC分类号： C12N15/113 ; A61K31/7125 ; A61K31/713 ; C07H21/02
摘要：
The present invention provides RNAi agents, e.g., double stranded RNAi agents, that target the transthyretin (TTR) gene and methods of using such RNAi agents for treating or preventing TTR-associated diseases.
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