Invention Grant
- Patent Title: mRNA for use in treatment of human genetic diseases
- Patent Title (中): 用于治疗人类遗传疾病的mRNA
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Application No.: US13306781Application Date: 2011-11-29
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Publication No.: US08853377B2Publication Date: 2014-10-07
- Inventor: Braydon Charles Guild , Michael Heartlein
- Applicant: Braydon Charles Guild , Michael Heartlein
- Applicant Address: US MA Lexington
- Assignee: Shire Human Genetic Therapies, Inc.
- Current Assignee: Shire Human Genetic Therapies, Inc.
- Current Assignee Address: US MA Lexington
- Agency: Choate, Hall & Stewart LLP
- Agent Fangli Chen
- Main IPC: C07H21/02
- IPC: C07H21/02 ; A61K9/127
Abstract:
Compositions for modulating the expression of a protein in a target cell comprising at least one RNA molecule which comprises at least one modification conferring stability to the RNA, as well as related methods, are disclosed.
Public/Granted literature
- US20120142756A1 mRNA FOR USE IN TREATMENT OF HUMAN GENETIC DISEASES Public/Granted day:2012-06-07
Information query
