发明申请
WO2015030616A3 USE OF NUCLEIC ACID MOLECULES IN THERAPY OF DISEASES INDUCED BY EXPANSION OF TRINUCLEOTIDE CAG REPEATS
审中-公开
核酸分子在扩展三核苷酸CAG重复序列所致疾病治疗中的应用
- 专利标题： USE OF NUCLEIC ACID MOLECULES IN THERAPY OF DISEASES INDUCED BY EXPANSION OF TRINUCLEOTIDE CAG REPEATS
- 专利标题（中）： 核酸分子在扩展三核苷酸CAG重复序列所致疾病治疗中的应用
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申请号： PCT/PL2014000100申请日： 2014-09-02
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公开(公告)号： WO2015030616A3公开(公告)日： 2015-09-03
- 发明人: KRZYZOSIAK WLODZIMIERZ , OLEJNICZAK MARTA , GALKA-MARCINIAK PAULINA , FISZER AGNIESZKA
- 申请人： INST CHEMII BIOORG PAN
- 专利权人： INST CHEMII BIOORG PAN
- 当前专利权人： INST CHEMII BIOORG PAN
- 优先权： PL40522413 2013-09-02
- 主分类号： C12N15/113
- IPC分类号： C12N15/113 ; A61K31/713 ; C12N5/10
摘要：
Subjects of the invention are: nucleic acid molecule, expression cassette, expression vector, eukaryotic host cell, induction method of RNA interference in eukaryotic host and use of nucleic acid molecule in therapy of diseases induced by expansion of trinucleotide CAG-type repeats. Solution relates to the new concept of treating hereditary human neurological diseases caused by expansion of CAG-type trinucleotide repeats using RNA interference technology.
公开/授权文献
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