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公开(公告)号:US10894960B2
公开(公告)日:2021-01-19
申请号:US15690526
申请日:2017-08-30
发明人: Assem G. Ziady , Matthew Siefert , Songbai Lin , Harrison Brown
IPC分类号: C12N15/113 , A61K38/17 , A61K47/60 , A61K47/64 , A61K31/713 , A61K31/395 , A61K31/4709 , A61K31/565 , A61K31/132 , A61K31/573 , A61K31/352 , A61K31/265 , A61K31/05 , A61K31/704 , A61K31/519 , A61K31/52 , A61K31/7048 , A61K48/00 , A61K31/7088 , C12N15/85 , A61K45/06 , C12N15/11 , A61K35/28
摘要: Disclosed are methods for the enhancement of nucleic acid delivery systems. The methods may employ treatment with a compound and/or an RNAi molecule in combination with a nucleic acid to improve nucleic acid uptake into a cell. In particular, the disclosed methods may be useful for improved gene therapy techniques.
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公开(公告)号:US20210102208A1
公开(公告)日:2021-04-08
申请号:US17121835
申请日:2020-12-15
发明人: Assem G. Ziady , Matthew Siefert , Songbai Lin , Harrison Brown
IPC分类号: C12N15/113 , A61K38/17 , A61K47/60 , A61K47/64 , A61K31/713 , A61K31/395 , A61K31/4709 , A61K31/565 , A61K31/132 , A61K31/573 , A61K31/352 , A61K31/265 , A61K31/05 , A61K31/704 , A61K31/519 , A61K31/52 , A61K31/7048 , A61K48/00 , A61K31/7088 , C12N15/85 , A61K45/06 , C12N15/11
摘要: Disclosed are methods for the enhancement of nucleic acid delivery systems. The methods may employ treatment with a compound and/or an RNAi molecule in combination with a nucleic acid to improve nucleic acid uptake into a cell. In particular, the disclosed methods may be useful for improved gene therapy techniques.
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公开(公告)号:US20180057813A1
公开(公告)日:2018-03-01
申请号:US15690526
申请日:2017-08-30
发明人: Assem G. Ziady , Matthew Siefert , Songbai Lin , Harrison Brown
IPC分类号: C12N15/113 , A61K38/17 , A61K35/28 , A61K47/60 , A61K47/64 , A61K31/713 , A61K31/395 , A61K31/4709 , A61K31/565 , A61K31/132 , A61K31/573 , A61K31/352 , A61K31/265 , A61K31/05 , A61K31/704 , A61K31/519 , A61K31/52 , A61K31/7048 , A61K48/00 , A61K31/7088 , C12N15/85
CPC分类号: C12N15/113 , A61K31/05 , A61K31/132 , A61K31/265 , A61K31/352 , A61K31/395 , A61K31/4709 , A61K31/519 , A61K31/52 , A61K31/565 , A61K31/573 , A61K31/704 , A61K31/7048 , A61K31/7088 , A61K31/713 , A61K35/28 , A61K38/1709 , A61K45/06 , A61K47/60 , A61K47/6455 , A61K48/0008 , A61K48/0066 , C12N15/111 , C12N15/85 , C12N2310/14 , C12N2320/31 , C12N2320/32
摘要: Disclosed are methods for the enhancement of nucleic acid delivery systems. The methods may employ treatment with a compound and/or an RNAi molecule in combination with a nucleic acid to improve nucleic acid uptake into a cell. In particular, the disclosed methods may be useful for improved gene therapy techniques.
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