- 专利标题： ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE CENTRAL NERVOUS SYSTEM
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申请号： EP19202040.2申请日： 2014-05-15
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公开(公告)号： EP3622821A1公开(公告)日： 2020-03-18
- 发明人: MCIVOR, R., Scott , BELUR, Lalitha R. , LOW, Walter , FAIRBANKS, Carolyn , KOZARSKY, Karen
- 申请人： Regents of the University of Minnesota , REGENXBIO Inc.
- 申请人地址： 600 McNamara Alumni Center 200 Oak St. SE Minneapolis, MN 55455 US
- 专利权人： Regents of the University of Minnesota,REGENXBIO Inc.
- 当前专利权人： Regents of the University of Minnesota,REGENXBIO Inc.
- 当前专利权人地址： 600 McNamara Alumni Center 200 Oak St. SE Minneapolis, MN 55455 US
- 代理机构： Gowshall, Jonathan Vallance
- 优先权： US201361823757P 20130515
- 主分类号： A01N63/00
- IPC分类号： A01N63/00 ; C12N15/00 ; C12N15/86
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.
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