Invention Publication
- Patent Title: RAAV-BASED COMPOSITIONS AND METHODS
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Application No.: US18426444Application Date: 2024-01-30
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Publication No.: US20240240180A1Publication Date: 2024-07-18
- Inventor: Terence Flotte , Christian Mueller , Phillip D. Zamore
- Applicant: University of Massachusetts
- Applicant Address: US MA Boston
- Assignee: University of Massachusetts
- Current Assignee: University of Massachusetts
- Current Assignee Address: US MA Boston
- Main IPC: C12N15/113
- IPC: C12N15/113 ; A61K31/713 ; A61K35/12 ; A61K38/57 ; A61K48/00 ; C07K14/81 ; C12N7/00 ; C12N15/67 ; C12N15/86 ; C12N15/11
Abstract:
The invention relates to isolated nucleic acids and rAAV-based compositions, methods and kits useful for treating genetic diseases (e.g., alpha-1 antitrypsin deficiency).
Information query
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