Invention Grant
- Patent Title: mRNA for use in treatment of human genetic diseases
- Patent Title (中): 用于治疗人类遗传疾病的mRNA
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Application No.: US14325594Application Date: 2014-07-08
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Publication No.: US09061021B2Publication Date: 2015-06-23
- Inventor: Braydon Charles Guild , Michael Heartlein , Frank DeRosa
- Applicant: Shire Human Genetic Therapies, Inc.
- Applicant Address: US MA Lexington
- Assignee: Shire Human Genetic Therapies, Inc.
- Current Assignee: Shire Human Genetic Therapies, Inc.
- Current Assignee Address: US MA Lexington
- Agency: Choate, Hall & Stewart LLP
- Agent Fangli Chen
- Main IPC: A61K48/00
- IPC: A61K48/00 ; A61K38/47 ; C07K14/505 ; C07K14/61 ; C12N15/67 ; C12N9/10 ; C12N9/40 ; A61K38/27 ; A61K38/45
Abstract:
Compositions for modulating the expression of a protein in a target cell comprising at least one RNA molecule which comprises at least one modification conferring stability to the RNA, as well as related methods, are disclosed.
Public/Granted literature
- US20150004217A1 mRNA FOR USE IN TREATMENT OF HUMAN GENETIC DISEASES Public/Granted day:2015-01-01
Information query
