专利检索 ap:("BioMarin Technologies B.V.") AND inv:"MULDERS, Susan Allegonda Maria" 第 1 页

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发明授权
RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders 有权
标题翻译：与用于治疗神经肌肉疾病改进的性能RNA调节寡核苷酸

公开(公告)号：EP2841578B1

公开(公告)日：2017-06-07

申请号：EP13720617.3

申请日：2013-04-23

申请人： BioMarin Technologies B.V.

发明人： DE VISSER, Peter Christian , MULDERS, Susan Allegonda Maria

IPC分类号： C12N15/113 , A61K31/7115 , A61K31/712 , A61K31/7125 , A61P25/00

CPC分类号： C12N15/113 , C12N2310/11 , C12N2310/315 , C12N2310/321 , C12N2310/333 , C12N2310/334 , C12N2310/3341 , C12N2310/335 , C12N2310/336 , C12N2310/346 , C12N2310/3521 , C12N2320/34

摘要： The current invention provides an improved oligonucleotide and its use for treating, ameliorating, preventing, delaying and/or treating a human cis-element repeat instability associated genetic neuromuscular or neurodegenerative disorder.

摘要翻译： 当前发明提供了改进的寡核苷酸和其用于治疗，改善，预防，延缓和/或治疗相关的遗传神经肌肉或神经变性病症的人顺式元件重复不稳定性的用途。