-
1.发明授权公开(公告)号：US11946065B2
公开(公告)日：2024-04-02
申请号：US17387035
申请日：2021-07-28
Inventor： Berge A. Minassian , Emrah Gumusgoz
IPC: C12N15/864 , C12N7/00 , C12N15/11 , C12N15/113 , C12N15/15 , C12N15/86
CPC classification number: C12N15/86 , C12N7/00 , C12N2750/14143 , C12N2750/14151
Abstract: The present disclosure provides methods and compositions for the treatment of diseases and genetic disorders linked to CSTB loss and/or misfunction. The methods and compositions of the present disclosure include rAAV vectors and rAAV viral vectors comprising transgene nucleic acid molecules encoding CSTB polypeptides.
Search Results
1
records
(took 0.026 seconds)
筛选
AND
AND
过滤
NOT
NOT
Scan to Join
