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公开(公告)号:US20210113634A1
公开(公告)日:2021-04-22
申请号:US17038031
申请日:2020-09-30
Applicant: BIOVERATIV THERAPEUTICS INC.
Inventor: Andrew Kroetsch , Isidro Zarraga
Abstract: Lentiviral vector (LV) formulations, and pharmaceutical compositions comprising such LV formulations, with improved stability and suitable for systemic administration are provided. Methods for treating disorders, especially blood disorders, using systemic administration of LV formulations are also provided.