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公开(公告)号:US20180353620A1
公开(公告)日:2018-12-13
申请号:US16109630
申请日:2018-08-22
申请人: EyeServ GmbH
CPC分类号: A61K48/0058 , A61K48/0066 , A61K48/0075 , A61P27/02 , C12N9/16 , C12N2750/14143 , C12N2799/025 , C12N2830/008
摘要: The present invention relates to a polynucleotide configured for the treatment of a retinal degeneration disease, such as retinitis pigmentosa (RP), a nucleic acid vector comprising said polynucleotide, a pharmaceutical composition comprising said nucleic acid vector, a kit comprising said polynucleotide or said nucleic acid vector, a method of making said nucleic acid vector, and a method for treating a retinal degeneration disease.