-
1.
公开(公告)号:US20240158792A1
公开(公告)日:2024-05-16
申请号:US18504781
申请日:2023-11-08
发明人: Tomonori UNO , Takashi NATSUKAWA , Youichi EGAWA , Youhei SATOU
IPC分类号: C12N15/113 , A61P21/00
CPC分类号: C12N15/113 , A61P21/00 , C12N2310/11 , C12N2320/35
摘要: The present invention relates to a composition containing an antisense oligonucleotide, and the use thereof to treat Duchenne muscular dystrophy. The present invention particularly relates to the above-described composition that is effective for the treatment of Duchenne muscular dystrophy when it is administered at a dose for the treatment, and the use thereof.
-
公开(公告)号:US20210261963A1
公开(公告)日:2021-08-26
申请号:US17253760
申请日:2019-06-26
发明人: Tomonori UNO , Takashi NATSUKAWA , Youichi EGAWA , Youhei SATOU
IPC分类号: C12N15/113 , A61P21/00
摘要: The present invention relates to a composition containing an antisense oligonucleotide, and the use thereof to treat Duchenne muscular dystrophy. The present invention particularly relates to the above-described composition that is effective for the treatment of Duchenne muscular dystrophy when it is administered at a dose for the treatment, and the use thereof.
-