公开(公告)号：WO2022271836A2

公开(公告)日：2022-12-29

申请号：PCT/US2022/034539

申请日：2022-06-22

申请人： ACURASTEM, INC.

发明人： CHANG, Wen-Hsuan ,  LEE, Emily Elizabeth

IPC分类号： C12N15/113 ,  A61P25/00 ,  A61K31/7115 ,  A61K31/712 ,  A61K31/7125 ,  A61K31/713 ,  C12N15/1137 ,  C12N2310/11 ,  C12N2310/31 ,  C12N2310/315 ,  C12N2310/321 ,  C12N2310/3341 ,  C12N2310/341 ,  C12N2310/345 ,  C12N2310/346 ,  C12N2320/32 ,  C12Y207/0115

摘要： The present invention relates to PIKFYVE antisense oligonucleotides (ASOs), pharmaceutical compositions containing them, and methods for treating, inhibiting, suppressing, and preventing neurological diseases with them.