- 专利标题: GENE MANIPULATION FOR TREATMENT OF RETINAL DYSFUNCTION DISORDER
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申请号: US16650993申请日: 2018-09-28
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公开(公告)号: US20200277630A1公开(公告)日: 2020-09-03
- 发明人: Dong Woo SONG , Jung Min LEE , Un Gi KIM , Jeong Hun KIM , Dong Hyun JO
- 申请人: TOOLGEN INCORPORATED , SEOUL NATIONAL UNIVERSITY R&DB FOUNDATION , SEOUL NATIONAL UNIVERSITY HOSPITAL
- 国际申请: PCT/KR2018/011522 WO 20180928
- 主分类号: C12N15/86
- IPC分类号: C12N15/86 ; C12N15/113 ; C12N9/22 ; A61P27/02
摘要:
The present invention relates to a composition for gene manipulation for treating or improving a retinal dysfunction disease or a method using the same. More particularly, the present invention relates to a composition for gene manipulation including a guide nucleic acid capable of targeting a retinal function-forming gene and a method of treating or improving a disease caused by retinal dysfunction by artificially manipulating and/or correcting a retinal function-forming gene using the same.
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