专利检索 ap:("The United States Of America as Represented by the Secretary, Department of Health an Human Service") AND inv:"VENDITTI, Charles, P." 第 1 页

1.

发明授权
VIRAL GENE THERAPY AS TREATMENT FOR CHOLESTEROL STORAGE DISEASE OR DISORDER 有权

公开(公告)号：EP3280451B1

公开(公告)日：2019-08-14

申请号：EP16717228.7

申请日：2016-04-07

申请人： The United States Of America as Represented by the Secretary, Department of Health an Human Service

发明人： VENDITTI, Charles, P. , PAVAN, William, J. , CHANDLER, Randy

IPC分类号： A61K48/00 , A61P25/28 , C12N15/864

2.

发明公开
VIRAL GENE THERAPY AS TREATMENT FOR CHOLESTEROL STORAGE DISEASE OR DISORDER 审中-公开
标题翻译：病毒基因疗法治疗胆固醇贮积症或失调症

公开(公告)号：EP3280451A1

公开(公告)日：2018-02-14

申请号：EP16717228.7

申请日：2016-04-07

申请人： The United States Of America as Represented by the Secretary, Department of Health an Human Service

发明人： VENDITTI, Charles, P. , PAVAN, William, J. , CHANDLER, Randy

IPC分类号： A61K48/00 , A61P25/28 , C12N15/864

CPC分类号： A61K35/761 , A61K48/005 , A61P3/00 , A61P25/28 , C07K14/075 , C12N7/04 , C12N15/86 , C12N15/8616 , C12N2710/10022 , C12N2710/10034 , C12N2710/10045 , C12N2750/14143

摘要： Provided herein are compositions and methods for the viral gene therapy (e.g., AAV-directed gene therapy) of cholesterol storage diseases or disorders, such as Niemann-Pick disease, Type C.