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公开(公告)号:US20140051748A1
公开(公告)日:2014-02-20
申请号:US13818956
申请日:2011-08-25
申请人: Asa Abeliovich , Hervé Rhinn , Toru Yamashita
发明人: Asa Abeliovich , Hervé Rhinn , Toru Yamashita
IPC分类号: C12N15/113
CPC分类号: C12N15/113 , C12N15/111 , C12N2310/141 , C12N2330/00
摘要: The invention provides optimized miRNA sequences and their therapeutic use. The invention provides optimized miRNA constructs for treatment of neurodegenerative diseases.
摘要翻译: 本发明提供优化的miRNA序列及其治疗用途。 本发明提供用于治疗神经变性疾病的优化的miRNA构建体。
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公开(公告)号:US09290759B2
公开(公告)日:2016-03-22
申请号:US13818956
申请日:2011-08-25
申请人: Asa Abeliovich , Hervé Rhinn , Toru Yamashita
发明人: Asa Abeliovich , Hervé Rhinn , Toru Yamashita
IPC分类号: C07H21/02 , C12N15/11 , C12N15/113
CPC分类号: C12N15/113 , C12N15/111 , C12N2310/141 , C12N2330/00
摘要: The invention provides optimized miRNA sequences and their therapeutic use. The invention provides optimized miRNA constructs for treatment of neurodegenerative diseases.
摘要翻译: 本发明提供优化的miRNA序列及其治疗用途。 本发明提供用于治疗神经变性疾病的优化的miRNA构建体。
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