Invention Grant
- Patent Title: Compositions and methods for treatment of homocystinuria
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Application No.: US15774755Application Date: 2016-11-09
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Publication No.: US10653755B2Publication Date: 2020-05-19
- Inventor: Jan P. Kraus , Tomas Majtan , Erez Bublil
- Applicant: THE REGENTS OF THE UNIVERSITY OF COLORADO, A BODY CORPORATE
- Applicant Address: US CO Denver
- Assignee: THE REGENTS OF THE UNIVERSITY OF COLORADO, A BODY CORPORATE
- Current Assignee: THE REGENTS OF THE UNIVERSITY OF COLORADO, A BODY CORPORATE
- Current Assignee Address: US CO Denver
- Agency: DT Ward, PC
- Agent Donna T. Ward; Samuel A. McMahon
- International Application: PCT/US2016/061050 WO 20161109
- International Announcement: WO2017/083327 WO 20170518
- Main IPC: A61K38/51
- IPC: A61K38/51 ; A61K31/385 ; A61K31/198 ; A61K47/60 ; C12N9/96 ; C12N9/88 ; A61K45/06 ; A61K9/00 ; A61K31/205

Abstract:
Provided are compositions and methods for enzyme replacement therapy using modified human cystathionine beta synthase (CBS) in the treatment of homocystinuria and related diseases and disorders.
Public/Granted literature
- US20180318404A1 COMPOSITIONS AND METHODS FOR TREATMENT OF HOMOCYSTINURIA Public/Granted day:2018-11-08
Information query
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