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1.
公开(公告)号:US20240124897A1
公开(公告)日:2024-04-18
申请号:US18362867
申请日:2023-07-31
Applicant: Intellia Therapeutics, Inc.
Inventor: Yong Chang , Seth C. Alexander , Kristy M. Wood , Arti Mahendra Prakash Kanjolia , Shobu Odate , Jessica Lynn Seitzer , Reynald Michael Lescarbeau , Walter Strapps
CPC classification number: C12N15/907 , C12N9/22 , C12N15/11 , A61K38/00 , C12N2310/20
Abstract: Compositions and methods for editing, e.g., introducing double-stranded breaks, within the TTR gene are provided. Compositions and methods for treating subjects having amyloidosis associated with transthyretin (ATTR), are provided.
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公开(公告)号:US20230044994A1
公开(公告)日:2023-02-09
申请号:US17486735
申请日:2021-09-27
Applicant: Intellia Therapeutics, Inc.
Inventor: Yong Chang , Seth C. Alexander , Kristy M. Wood , Arti Mahendra Prakash Kanjolia , Shobu Odate , Jessica Lynn Seitzer , Reynald Michael Lescarbeau , Walter Strapps
Abstract: Compositions and methods for editing, e.g., introducing double-stranded breaks, within the TTR gene are provided. Compositions and methods for treating subjects having amyloidosis associated with transthyretin (ATTR), are provided.
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