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1.
公开(公告)号:US20180044286A1
公开(公告)日:2018-02-15
申请号:US15549743
申请日:2016-02-11
发明人: Samarjit PATNAIK , Mercedes TAYLOR , Raul Rolando CALVO , Juan Jose MARUGAN , Noel SOUTHALL , Wei ZHENG , Marc FERRER-ALEGRE , Seameen DEHDASTHI , Patricia DRANCHAK , Fannie CHEN , Yiannis IOANNOU
IPC分类号: C07C311/21 , C07D207/335 , C07D213/46 , C07D233/64
CPC分类号: C07C311/21 , A61K31/165 , A61K31/4164 , A61K31/44 , C07D207/335 , C07D213/46 , C07D233/64
摘要: Methods and compositions for treating lysosomal storage disorders are disclosed. The methods involve administering a genus of benzenesulfonamides, particularly N-[3-(aminosulfonyl)phenyl]-benzamides and heteroarylamides. A genus of suitable compounds is shown in formula 1: